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Travere Therapeutics
Travere Therapeutics
(TVTX)
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Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Kolbam
Cholic acid
2015-11-20
Zellweger syndrome
,
Inborn errors metabolism
Syntocinon
Oxytocin
1982-01-01
Postpartum hemorrhage
Filspari
Sparsentan
2023-02-17
2030
Proteinuria
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Sparsentan
healthy volunteers/patients
,
renal insufficiency
,
smoldering multiple myeloma
,
lymphoma
,
leukemia
,
paraproteinemias
,
monoclonal gammopathy of undetermined significance
,
hypertension
,
precursor cell lymphoblastic leukemia-lymphoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
vasculitis
,
plasma cell leukemia
,
residual neoplasm
,
syndrome
,
poems syndrome
,
non-hodgkin lymphoma
,
hodgkin disease
,
anemia
,
aplastic anemia
,
pancytopenia
,
bone marrow failure disorders
,
b-cell lymphoma
,
b-cell leukemia
,
glomerulonephritis
,
immune system diseases
,
autoimmune diseases
,
iga vasculitis
,
hereditary nephritis
,
lipoid nephrosis
,
cardiovascular diseases
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
hematopoietic stem cell transplantation
,
amyloidosis
,
iga glomerulonephritis
,
immunoglobulin light-chain amyloidosis
,
kidney diseases
,
focal segmental glomerulosclerosis
,
multiple myeloma
,
plasma cell neoplasms
,
coronary artery disease
,
recurrence
Angiotensin ii
pre-eclampsia
,
therapeutic equivalency
,
malnutrition
,
autonomic nervous system diseases
,
pure autonomic failure
,
orthostatic hypotension
,
primary dysautonomias
,
prostatic neoplasms
,
carcinoma
,
peripheral vascular diseases
,
pharmacokinetics
,
shy-drager syndrome
,
multiple system atrophy
,
postural orthostatic tachycardia syndrome
,
tachycardia
,
arteriovenous fistula
,
fistula
,
iga vasculitis
,
purpura
,
myelodysplastic syndromes
,
castration-resistant prostatic neoplasms
,
precursor cell lymphoblastic leukemia-lymphoma
,
b-cell chronic lymphocytic leukemia
,
bcr-abl positive chronic myelogenous leukemia
,
myelomonocytic leukemia chronic
,
anemia
,
leukemia myeloid chronic atypical bcr-abl negative
,
myelodysplastic-myeloproliferative diseases
,
myeloid leukemia chronic-phase
,
myeloid leukemia accelerated phase
,
myelomonocytic leukemia juvenile
,
preleukemia
,
blast crisis
,
thrombocytosis
,
lymphoid leukemia
,
magnetic resonance imaging
,
oral administration
,
obstructive lung diseases
,
barrett esophagus
,
nervous system diseases
,
polycystic ovary syndrome
,
hyperphosphatemia
,
fasting
,
substance-related disorders
,
lung diseases
,
disease
,
pancreatic ductal carcinoma
,
sex characteristics
,
squamous cell carcinoma of head and neck
,
squamous cell carcinoma
,
social cognition
,
affect
,
pancreatic neoplasms
,
aging
,
sickle cell anemia
,
headache
,
adenocarcinoma
,
hematologic neoplasms
,
acquired immunodeficiency syndrome
,
post-traumatic stress disorders
,
radiation fibrosis syndrome
,
nephrotic syndrome
,
nephrosis
,
peripheral nervous system diseases
,
cystic fibrosis
,
traumatic stress disorders
,
non-small-cell lung carcinoma
,
radiation pneumonitis
,
hereditary nephritis
,
traumatic brain injuries
,
brain injuries
,
respiratory insufficiency
,
hepatorenal syndrome
,
osteosarcoma
,
leukemia
,
myeloid leukemia acute
,
myeloproliferative disorders
,
primary myelofibrosis
,
multiple myeloma
,
hodgkin disease
,
plasma cell neoplasms
,
myeloid leukemia
,
neoplasm metastasis
,
melanoma
,
vascular diseases
,
arthritis
,
neuralgia
,
eosinophilic esophagitis
,
esophagitis
,
pulmonary arterial hypertension
,
sarcopenia
,
right ventricular dysfunction
,
arthrogryposis
,
graft vs host disease
,
cardio-renal syndrome
,
sarcoma
,
dyspnea
,
colorectal neoplasms
,
small cell lung carcinoma
,
ovarian neoplasms
,
ovarian epithelial carcinoma
,
knee osteoarthritis
,
osteoarthritis
,
myositis
,
pheochromocytoma
,
hip osteoarthritis
,
metabolism
,
energy metabolism
,
brain neoplasms
,
psychotic affective disorders
,
mood disorders
,
treatment-resistant schizophrenia
,
mucopolysaccharidosis iv
,
mucopolysaccharidosis vi
,
mucopolysaccharidoses
,
mucopolysaccharidosis i
,
osteochondrodysplasias
,
intracranial hypertension
,
pain
,
sedentary behavior
,
postherpetic neuralgia
,
pulmonary vein stenosis
,
macular edema
,
edema
,
psychological stress
,
ebola hemorrhagic fever
,
virus diseases
,
congenital abnormalities
,
tetralogy of fallot
,
cocaine-related disorders
,
bone neoplasms
,
chondrosarcoma
,
clear cell sarcoma
,
alcoholic liver diseases
,
chronic disease
,
hermanski-pudlak syndrome
,
oculocutaneous albinism
,
platelet storage pool deficiency
,
albinism
,
carotid artery diseases
,
cluster headache
,
parkinson disease
,
multiple sclerosis
,
coronavirus
,
opioid-related disorders
,
sleep initiation and maintenance disorders
,
chronic pain
,
brain diseases
,
amyotrophic lateral sclerosis
,
epilepsy
,
inflammatory bowel diseases
,
glaucoma
,
tourette syndrome
,
fibromyalgia
,
motor neuron disease
,
seizures
,
chronic traumatic encephalopathy
,
sclerosis
,
autistic disorder
,
anxiety
,
male breast neoplasms
,
body weight
,
immunoglobulin light-chain amyloidosis
,
pseudohypoaldosteronism
,
acoustic neuroma
,
neuroma
,
neurilemmoma
,
endocardial fibroelastosis
,
dementia
,
renal dialysis
,
gastrointestinal neoplasms
,
stomatitis
,
drug therapy
,
mucositis
,
keloid
,
replacement arthroplasty knee
,
panic disorder
,
knee injuries
,
marfan syndrome
,
arachnodactyly
,
hypertrophic cardiomyopathy
,
pulmonary fibrosis
,
pulmonary hypertension
,
hemorrhage
,
cerebral hemorrhage
,
alzheimer disease
,
lung neoplasms
,
idiopathic pulmonary fibrosis
,
vasoplegia
,
toxemia
,
cardiac arrhythmias
,
migraine disorders
,
pneumonia
,
metabolic diseases
,
inferior wall myocardial infarction
,
cerebral small vessel diseases
,
kidney transplantation
,
congenital heart defects
,
disease progression
,
hyperkalemia
,
arterial occlusive diseases
,
severe acute respiratory syndrome-related coronavirus
,
glioblastoma
,
vascular dementia
,
hypertriglyceridemia
,
bicuspid aortic valve disease
,
pathologic dilatation
,
oxidative stress
,
microvascular angina
,
amyloidosis
,
st elevation myocardial infarction
,
cardiac surgical procedures
,
hemorrhagic stroke
,
transcatheter aortic valve replacement
,
heart valve prosthesis implantation
,
ehlers-danlos syndrome
,
type iv ehlers-danlos syndrome
,
aortic valve disease
,
migraine without aura
,
migraine with aura
,
metabolic brain diseases
,
hyperoxaluria
,
primary hyperoxaluria
,
renovascular hypertension
,
renal artery obstruction
,
chagas cardiomyopathy
,
myocarditis
,
sudden death cardiac
,
death
,
exercise tolerance
,
aortic coarctation
,
hypertension
,
essential hypertension
,
heart failure
,
healthy volunteers/patients
,
kidney diseases
,
diabetes mellitus
,
type 2 diabetes mellitus
,
diabetic nephropathies
,
syndrome
,
chronic renal insufficiency
,
covid-19
,
cardiovascular diseases
,
proteinuria
,
obesity
,
hyperlipidemias
,
metabolic syndrome
,
hypertrophy
,
renal insufficiency
,
fibrosis
,
dyslipidemias
,
insulin resistance
,
stroke
,
atrial fibrillation
,
heart diseases
,
left ventricular hypertrophy
,
shock
,
iga glomerulonephritis
,
myocardial infarction
,
infarction
,
cardiomyopathies
,
coronary artery disease
,
albuminuria
,
septic shock
,
myocardial ischemia
,
infections
,
coronavirus infections
,
systolic murmurs
,
inflammation
,
glomerulonephritis
,
hypercholesterolemia
,
chronic kidney failure
,
atherosclerosis
,
communicable diseases
,
acute kidney injury
,
hypotension
,
neoplasms
,
breast neoplasms
,
hiv infections
,
hyperlipoproteinemias
,
sepsis
,
ventricular remodeling
,
blood pressure
,
ischemia
,
acute lung injury
,
sleep apnea syndromes
,
ischemic stroke
,
respiratory distress syndrome
,
newborn respiratory distress syndrome
,
left ventricular dysfunction
,
severe acute respiratory syndrome
,
apnea
,
recurrence
,
cognitive dysfunction
,
type 1 diabetes mellitus
,
isolated systolic hypertension
,
systolic heart failure
,
ventricular dysfunction
,
nephritis
,
wounds and injuries
,
hypersensitivity
,
glucose intolerance
,
coronary disease
,
liver diseases
,
liver cirrhosis
,
renin-angiotensin system
,
cardiotoxicity
,
obstructive sleep apnea
,
cerebral infarction
,
non-alcoholic fatty liver disease
,
fatty liver
,
pathologic constriction
,
overweight
,
prediabetic state
,
aortic valve stenosis
,
focal segmental glomerulosclerosis
,
peripheral arterial disease
,
mitral valve insufficiency
,
polycystic kidney diseases
,
atrial remodeling
,
membranous glomerulonephritis
,
depression
,
depressive disorder
,
diastolic heart failure
,
lymphoma
,
schizophrenia
,
dilated cardiomyopathy
,
aneurysm
,
hepatitis c
,
acute coronary syndrome
,
diabetic retinopathy
,
sars-cov-2
,
bipolar disorder
,
drug-related side effects and adverse reactions
,
non-hodgkin lymphoma
,
psychotic disorders
,
stable angina
,
hypoxia
,
chronic obstructive pulmonary disease
,
angina pectoris
,
autosomal dominant polycystic kidney
,
drug interactions
,
aortic aneurysm
,
prehypertension
,
chronic hepatitis c
,
hepatitis
,
hepatitis a
,
retinal diseases
,
low cardiac output
,
connective tissue diseases
,
hyperaldosteronism
,
aortic valve insufficiency
,
diabetic neuropathies
,
ulcerative colitis
,
crohn disease
,
emphysema
,
pulmonary emphysema
,
chronic bronchitis
,
bronchitis
,
major depressive disorder
,
mental disorders
,
abdominal aortic aneurysm
,
abdominal obesity
,
vascular remodeling
,
carotid stenosis
,
arteriosclerosis
,
endomyocardial fibrosis
,
end stage liver disease
,
surgical shock
,
respiratory tract diseases
,
respiration disorders
,
cardiogenic shock
,
chagas disease
,
peritoneal dialysis
,
respiratory aspiration
,
sleep wake disorders
,
pharmacogenomic testing
,
colitis
,
ulcer
,
vitamin d deficiency
,
osteoporosis
,
postoperative pain
,
acute disease
,
intermittent claudication
,
altitude sickness
,
graft rejection
,
white coat hypertension
,
nephrolithiasis
,
kidney calculi
,
calculi
,
physiological sexual dysfunction
,
nephrosclerosis
,
continuous ambulatory peritoneal dialysis
,
smoking
,
erectile dysfunction
,
hyperglycemia
,
cardiopulmonary bypass
,
fibrinolysis
,
cardiac volume
,
chronic hepatitis
,
liver transplantation
,
alcoholic liver cirrhosis
,
ascites
,
rectal diseases
,
brain infarction
,
diabetic angiopathies
,
hypokalemia
,
second primary neoplasms
,
breast diseases
,
athletic injuries
,
systemic inflammatory response syndrome
,
hyperuricemia
,
morbid obesity
,
eclampsia
,
vasodilation
,
pediatric obesity
,
pregnancy-induced hypertension
,
aortic dissection
,
sick sinus syndrome
,
cough
,
microcirculation
,
neurologic manifestations
,
frailty
,
minoca
,
thrombosis
,
thrombophilia
,
venous thrombosis
,
intracranial thrombosis
,
heart disease risk factors
,
urologic diseases
,
adenoma
,
hematopoietic stem cell transplantation
,
memory
,
learning
,
ambulatory blood pressure monitoring
,
vascular stiffness
,
lupus nephritis
,
hypophosphatemia
,
familial hypophosphatemic rickets
,
gender role
,
lung injury
,
hiv
,
adrenocortical adenoma
,
adrenal gland neoplasms
,
rheumatoid arthritis
,
duchenne muscular dystrophy
,
muscular dystrophies
,
diabetes complications
,
thoracic aortic aneurysm
,
heart valve diseases
,
long-term memory
,
short-term memory
,
hypoglycemia
,
exercise
,
precancerous conditions
,
cohort studies
,
glucose metabolism disorders
,
fabry disease
,
drug dose-response relationship
,
orthostatic intolerance
,
hematuria
,
secondary headache disorders
,
prescription drug overuse
,
post-traumatic headache
,
post-concussion syndrome
,
morals
,
univentricular heart
,
medication adherence
,
bone fractures
,
colonic neoplasms
Fosmetpantotenate
nerve degeneration
,
pantothenate kinase-associated neurodegeneration
Lornoxicam
female genital neoplasms
,
nervous system diseases
,
adrenocortical carcinoma
,
pregnancy
,
antiphospholipid syndrome
,
juvenile arthritis
,
analgesia
,
gastrointestinal stromal tumors
,
uveal melanoma
,
immunoglobulin g4-related disease
,
bile duct neoplasms
,
pharmacokinetics
,
pheochromocytoma
,
paraganglioma
,
deltaretrovirus infections
,
htlv-i infections
,
composite lymphoma
,
eyelid diseases
,
osteogenesis imperfecta
,
neuroepithelial neoplasms
,
pharyngeal neoplasms
,
male genital neoplasms
,
poems syndrome
,
smooth muscle tumor
,
papillary thyroid cancer
,
medullary carcinoma
,
ganglioglioma
,
ischemia
,
peripheral arterial disease
,
peripheral vascular diseases
,
carcinoid tumor
,
skin diseases
,
adrenal cortex neoplasms
,
papillomaviridae
,
papilloma
,
gout
,
ovarian diseases
,
abdominal neoplasms
,
lymphocytosis
,
small cell carcinoma
,
neuromuscular manifestations
,
demyelinating diseases
,
cns demyelinating autoimmune diseases
,
transplantation tolerance
,
stomach neoplasms
,
liver neoplasms
,
prostatic neoplasms
,
hepatocellular carcinoma
,
uterine cervical neoplasms
,
skin neoplasms
,
glioblastoma
,
glioma
,
prolymphocytic leukemia
,
mesothelioma
,
esophageal neoplasms
,
head and neck neoplasms
,
squamous cell neoplasms
,
malignant mesothelioma
,
myeloid leukemia accelerated phase
,
adult t-cell leukemia-lymphoma
,
residual neoplasm
,
mycoses
,
blast crisis
,
t-cell lymphoma cutaneous
,
mycosis fungoides
,
myxoid liposarcoma
,
plasma cell leukemia
,
aids-related lymphoma
,
lymphomatoid granulomatosis
,
castration-resistant prostatic neoplasms
,
crohn disease
,
chronic granulomatous disease
,
anus neoplasms
,
colonic neoplasms
,
invasive hydatidiform mole
,
rheumatoid arthritis
,
arthritis
,
cholangiocarcinoma
,
diffuse intrinsic pontine glioma
,
nasopharyngeal carcinoma
,
nasopharyngeal neoplasms
,
rectal neoplasms
,
prolymphocytic leukemia t-cell
,
thyroid neoplasms
,
astrocytoma
,
sezary syndrome
,
endometrial neoplasms
,
reactive arthritis
,
gastrointestinal neoplasms
,
myasthenia gravis
,
precancerous conditions
,
intestinal neoplasms
,
uveal neoplasms
,
primary immunodeficiency diseases
,
muscular diseases
,
urologic neoplasms
,
merkel cell carcinoma
,
thymus neoplasms
,
hairy cell leukemia
,
intraocular lymphoma
,
metabolic diseases
,
neuroendocrine tumors
,
kidney transplantation
,
granuloma
,
thyroid diseases
,
oropharyngeal neoplasms
,
pancreatic ductal carcinoma
,
disease progression
,
serous cystadenocarcinoma
,
muscle weakness
,
immunosuppression therapy
,
blastic plasmacytoid dendritic cell neoplasm
,
common variable immunodeficiency
,
polycythemia vera
,
polycythemia
,
bone fractures
,
vulvar neoplasms
,
penile neoplasms
,
castleman disease
,
primary effusion lymphoma
,
desmoplastic small round cell tumor
,
thymoma
,
wiskott-aldrich syndrome
,
intestinal diseases
,
healthy volunteers/patients
,
hepatitis b
,
precursor b-cell lymphoblastic leukemia-lymphoma
,
autoimmune diseases of the nervous system
,
large granular lymphocytic leukemia
,
vaginal neoplasms
,
gliosarcoma
,
germinoma
,
adenocarcinoma of lung
,
pinealoma
,
iga vasculitis
,
hypertension
,
gata2 deficiency
,
hepatoblastoma
,
essential thrombocythemia
,
thrombocytosis
,
x-linked combined immunodeficiency diseases
,
adenosquamous carcinoma
,
vitamin d deficiency
,
digestive system neoplasms
,
epstein-barr virus infections
,
pure red-cell aplasia
,
hemolytic anemia autoimmune
,
hemolytic anemia
,
chronic inflammatory demyelinating polyradiculoneuropathy
,
type 1 diabetes mellitus
,
oligodendroglioma
,
cord blood stem cell transplantation
,
graft rejection
,
microsatellite instability
,
transitional cell carcinoma
,
carcinoma in situ
,
hemangiosarcoma
,
malignant pleural effusion
,
endodermal sinus tumor
,
cytopenia
,
prolymphocytic leukemia b-cell
,
cardiovascular diseases
,
hepatitis
,
liver transplantation
,
encephalitis
,
meningioma
,
metabolic syndrome
,
autoimmune lymphoproliferative syndrome
,
pulmonary hypertension
,
epidermolysis bullosa
,
neuroendocrine carcinoma
,
mucopolysaccharidosis vi
,
mucopolysaccharidosis i
,
alpha-mannosidosis
,
mannosidase deficiency diseases
,
inborn genetic diseases
,
glandular and epithelial neoplasms
,
urogenital neoplasms
,
endocrine gland neoplasms
,
stiff-person syndrome
,
immunoproliferative disorders
,
hemolysis
,
neoplasms by histologic type
,
myoepithelioma
,
immunotherapy
,
cell- and tissue-based therapy
,
adoptive immunotherapy
,
monoclonal gammopathy of undetermined significance
,
brain diseases
,
endometrioid carcinoma
,
cystadenocarcinoma
,
breast carcinoma in situ
,
teratoma
,
choriocarcinoma
,
embryonal carcinoma
,
cytokine release syndrome
,
homologous transplantation
,
smoldering multiple myeloma
,
fatigue
,
treatment refusal
,
pain
,
focal segmental glomerulosclerosis
,
metabolic brain diseases
,
hiv seropositivity
,
leukopenia
,
mastocytosis
,
mucopolysaccharidosis vii
,
aspartylglucosaminuria
,
sphingolipidoses
,
nijmegen breakage syndrome
,
lymphatic diseases
,
thrombasthenia
,
polyneuropathies
,
disease
,
biliary tract neoplasms
,
alzheimer disease
,
polyradiculoneuropathy
,
papillomavirus infections
,
experimental melanoma
,
mesenchymal stem cell transplantation
,
migraine disorders
,
radiotherapy
,
hiv-2
,
central nervous system vasculitis
,
chordoma
,
uterine neoplasms
,
clear cell adenocarcinoma
,
acinar cell carcinoma
,
lobular carcinoma
,
thoracic neoplasms
,
clonal hematopoiesis
,
aneuploidy
,
autologous transplantation
,
non-gestational choriocarcinoma
,
antineoplastic combined chemotherapy protocols
,
appendiceal neoplasms
,
neoplasms by site
,
myc genes
,
congenital abnormalities
,
gene rearrangement
,
conjunctival neoplasms
,
deficiency diseases
,
pneumocephalus
,
mast-cell leukemia
,
necrosis
,
supratentorial neoplasms
,
basal cell carcinoma
,
basal cell nevus syndrome
,
monosomy
,
leukemia myeloid chronic atypical bcr-abl negative
,
graft survival
,
neutrophilic leukemia chronic
,
hypereosinophilic syndrome
,
eosinophilic leukemia acute
,
job syndrome
,
mucopolysaccharidosis ii
,
peroxisomal disorders
,
systemic mastocytosis
,
erythema
,
combination drug therapy
,
hereditary breast and ovarian cancer syndrome
,
prosthesis failure
,
pleural diseases
,
heart diseases
,
mucinous cystadenocarcinoma
,
hyperglycemia
,
chronic fatigue syndrome
,
myalgia
,
encephalomyelitis
,
metaplasia
,
frontotemporal dementia
,
type b niemann-pick disease
,
primary progressive aphasia
,
mucolipidoses
,
adenocarcinoma in situ
,
experimental neoplasms
,
malnutrition
,
depression
,
gastrointestinal diseases
,
diarrhea
,
felty syndrome
,
radiation effects
,
bunion
,
orthopedic procedures
,
sarcoidosis
,
gallbladder neoplasms
,
oral lichen planus
,
unilateral breast neoplasms
,
vulvar diseases
,
cervical intraepithelial neoplasia
,
uterine cervical dysplasia
,
anaplastic thyroid carcinoma
,
giant cell tumor of bone
,
giant cell tumors
,
squamous intraepithelial lesions
,
headache
,
intractable pain
,
metabolic brain diseases inborn
,
antibiotic prophylaxis
,
measles
,
ischemic stroke
,
stroke
,
cerebral infarction
,
paresis
,
infarction
,
paralysis
,
heterologous transplantation
,
pulpitis
,
endodontics
,
eyelid neoplasms
,
blood protein disorders
,
respiratory aspiration
,
cystinosis
,
aneurysm
,
chimera
,
fasting
,
extranodal extension
,
li-fraumeni syndrome
,
p53 genes
,
polymyositis
,
olfactory esthesioneuroblastoma
,
splenomegaly
,
invasive fungal infections
,
duodenal neoplasms
,
probiotics
,
pseudomyxoma peritonei
,
behavior therapy
,
neoplasms
,
myeloid leukemia acute
,
myeloid leukemia
,
hematologic neoplasms
,
melanoma
,
carcinoma
,
bcr-abl positive chronic myelogenous leukemia
,
ovarian neoplasms
,
myeloproliferative disorders
,
lung neoplasms
,
non-small-cell lung carcinoma
,
neoplasm metastasis
,
pancreatic neoplasms
,
ovarian epithelial carcinoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
colorectal neoplasms
,
b-cell lymphoma marginal zone
,
myelodysplastic-myeloproliferative diseases
,
central nervous system neoplasms
,
renal cell carcinoma
,
adenocarcinoma
,
biphenotypic leukemia acute
,
myelomonocytic leukemia chronic
,
ewing sarcoma
,
primary myelofibrosis
,
fallopian tube neoplasms
,
kidney neoplasms
,
autoimmune diseases
,
sickle cell anemia
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nervous system neoplasms
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brain neoplasms
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squamous cell carcinoma
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t-cell leukemia
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acute disease
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osteosarcoma
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multiple sclerosis
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inflammatory breast neoplasms
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large-cell lymphoma immunoblastic
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immunologic deficiency syndromes
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neuroectodermal tumors
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plasmablastic lymphoma
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fanconi anemia
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synovial sarcoma
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myositis
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ependymoma
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liposarcoma
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bone marrow failure disorders
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fanconi syndrome
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extranodal nk-t-cell lymphoma
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peritoneal neoplasms
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myelomonocytic leukemia acute
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cutaneous malignant melanoma
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refractory anemia with excess of blasts
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retinoblastoma
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small cell lung carcinoma
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immune system diseases
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drug-related side effects and adverse reactions
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embryonal rhabdomyosarcoma
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classical conditioning
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primitive neuroectodermal tumors peripheral
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pathologic complete response
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paroxysmal hemoglobinuria
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refractory anemia
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alveolar rhabdomyosarcoma
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cerebrotendinous xanthomatosis
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hemoglobinopathies
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second primary neoplasms
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hemoglobinuria
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hemophagocytic lymphohistiocytosis
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stem cell transplantation
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clear cell sarcoma
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testicular neoplasms
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peripheral blood stem cell transplantation
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relapsing-remitting multiple sclerosis
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purpura
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mucinous adenocarcinoma
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ganglioneuroblastoma
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chemotherapy-induced febrile neutropenia
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peripheral nervous system diseases
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cognitive dysfunction
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erythroblastic leukemia acute
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phenylketonurias
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langerhans-cell histiocytosis
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bone neoplasms
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chondrosarcoma
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fibrosarcoma
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benign fibrous histiocytoma
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histiocytoma
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brain stem neoplasms
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chronic progressive multiple sclerosis
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neuromyelitis optica
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megakaryoblastic leukemia acute
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diamond-blackfan anemia
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inflammation
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drug therapy
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malaria
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arteritis
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takayasu arteritis
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aortic arch syndromes
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severe combined immunodeficiency
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chediak-higashi syndrome
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osteopetrosis
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nephrotic syndrome
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nephrosis
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thrombocytopenic purpura
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down syndrome
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mouth neoplasms
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malignant fibrous histiocytoma
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mesenchymal chondrosarcoma
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behcet syndrome
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breast diseases
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ductal carcinoma
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neurotoxicity syndromes
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fever
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inborn errors metabolism
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mucopolysaccharidoses
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fucosidosis
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globoid cell leukodystrophy
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adrenoleukodystrophy
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dyskeratosis congenita
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shwachman-diamond syndrome
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pulmonary blastoma
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trophoblastic neoplasms
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therapeutics
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alveolar soft part sarcoma
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neurofibrosarcoma
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nerve sheath neoplasms
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mullerian mixed tumor
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chemotherapy-related cognitive impairment
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ocular motility disorders
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myoclonus
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opsoclonus-myoclonus syndrome
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mucositis
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choroid plexus neoplasms
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gestational trophoblastic disease
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metachromatic leukodystrophy
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idiopathic pulmonary fibrosis
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unknown primary neoplasms
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eosinophilic granuloma
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tuberculosis
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niemann-pick diseases
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type a niemann-pick disease
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wolman disease
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pick disease of the brain
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connective tissue diseases
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whole-body irradiation
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hyperthermia
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circulating neoplastic cells
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anti-glomerular basement membrane disease
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adolescent development
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hematopoietic stem cell mobilization
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postoperative complications
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bone marrow diseases
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leiomyosarcoma
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perivascular epithelioid cell neoplasms
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glomus tumor
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granular cell tumor
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cognition
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scleritis
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hearing loss
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sensorineural hearing loss
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lipoid nephrosis
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adjuvant chemotherapy
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bullous pemphigoid
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benign mucous membrane pemphigoid
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meningeal tuberculosis
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meningitis
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arachnoiditis
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retinal neoplasms
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mesenchymoma
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inguinal hernia
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hernia
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mixed connective tissue disease
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neuronal ceroid-lipofuscinoses
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tay-sachs disease
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sandhoff disease
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gm1 gangliosidosis
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gaucher disease
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gangliosidoses
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stomatitis
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acute kidney injury
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rheumatic diseases
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collagen diseases
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warts
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condylomata acuminata
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thrombosis
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positron-emission tomography
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hemorrhoids
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precursor cell lymphoblastic leukemia-lymphoma
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non-hodgkin lymphoma
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myelodysplastic syndromes
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b-cell chronic lymphocytic leukemia
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preleukemia
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recurrence
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triple negative breast neoplasms
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mantle-cell lymphoma
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t-cell lymphoma
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sarcoma
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neuroblastoma
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t-cell lymphoma peripheral
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graft vs host disease
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anemia
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plasmacytoma
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aplastic anemia
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systemic lupus erythematosus
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burkitt lymphoma
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nephritis
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myelomonocytic leukemia juvenile
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sclerosis
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systemic scleroderma
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lupus nephritis
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waldenstrom macroglobulinemia
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hematopoietic stem cell transplantation
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diffuse scleroderma
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vasculitis
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large-cell lymphoma anaplastic
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rhabdomyosarcoma
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kidney diseases
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medulloblastoma
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neutropenia
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philadelphia chromosome
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germ cell and embryonal neoplasms
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amyloidosis
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lymphoproliferative disorders
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myeloid leukemia chronic-phase
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anti-neutrophil cytoplasmic antibody-associated vasculitis
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primitive neuroectodermal tumors
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immunoblastic lymphadenopathy
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vomiting
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membranous glomerulonephritis
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osteoporosis
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immunoglobulin light-chain amyloidosis
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hiv infections
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nausea
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renal insufficiency
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male breast neoplasms
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aggression
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granulomatosis with polyangiitis
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thalassemia
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wilms tumor
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enteropathy-associated t-cell lymphoma
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cardiotoxicity
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neoadjuvant therapy
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microscopic polyangiitis
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iga glomerulonephritis
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glomerulonephritis
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systemic vasculitis
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lung diseases
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localized scleroderma
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beta-thalassemia
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infections
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acquired immunodeficiency syndrome
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interstitial lung diseases
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urinary bladder neoplasms
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diabetes mellitus
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hiv
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churg-strauss syndrome
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metabolic bone diseases
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pemphigus
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sjogren's syndrome
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myeloid sarcoma
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bronchiolitis obliterans syndrome
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postoperative pain
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postmenopausal osteoporosis
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febrile neutropenia
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type 2 diabetes mellitus
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communicable diseases
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hemophilia a
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panniculitis
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polyarteritis nodosa
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obesity
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menopause
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dermatomyositis
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human herpesvirus 8
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uveitis
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virus diseases
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glycogen storage disease type ii
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edema
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pneumonia
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acute coronary syndrome
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mediastinal neoplasms
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glycogen storage disease type iii
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glycogen storage disease
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kaposi sarcoma
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intravesical administration
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cystitis
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non-muscle invasive bladder neoplasms
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retroperitoneal fibrosis
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acute pain
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trismus
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arthralgia
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bone resorption
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knee osteoarthritis
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osteoarthritis
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inflammatory bowel diseases
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hemoglobin sc disease
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type 1 hyper-igm immunodeficiency syndrome
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hyper-igm immunodeficiency syndrome
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alopecia areata
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alopecia
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bone diseases
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periodontitis
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cytomegalovirus infections
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hemoglobin c disease
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taste disorders
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dysgeusia
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ageusia
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ataxia
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ataxia telangiectasia
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telangiectasis
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cerebellar ataxia
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hypoparathyroidism
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pregnancy rate
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defense mechanisms
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proteinuria
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ototoxicity
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leukocyte-adhesion deficiency syndrome
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hereditary congenital and neonatal diseases and abnormalities
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radius fractures
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bariatric surgery
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gastric bypass
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gastrectomy
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premenopause
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osteoporotic fractures
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hashimoto disease
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giant cell arteritis
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polymyalgia rheumatica
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hypersensitivity
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leukocytoclastic vasculitis cutaneous
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chronic disease
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cerebrovascular disorders
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pituitary neoplasms
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sex cord-gonadal stromal tumors
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sertoli-leydig cell tumor
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nodular goiter
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hyperplasia
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pituitary diseases
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leydig cell tumor
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focal nodular hyperplasia
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hamartoma
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body weight
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gastroenteritis
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autonomic nervous system diseases
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primary dysautonomias
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hypoventilation
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lipodystrophy
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hyponatremia
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anorexia
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anorexia nervosa
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bone density
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nerve compression syndromes
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tooth diseases
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charcot-marie-tooth disease
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hereditary sensory and motor neuropathy
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primary graft dysfunction
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renal colic
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colic
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cataract
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anxiety disorders
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microbiota
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congenital bone marrow failure syndromes
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undiagnosed diseases
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eye abnormalities
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uveomeningoencephalitic syndrome
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tumor microenvironment
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wounds and injuries
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spinal cord injuries
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echocardiography
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hyperspectral imaging
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primary ovarian insufficiency
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premature menopause
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hip fractures
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femoral neck fractures
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chronic pain
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muscle neoplasms
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cystic fibrosis
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laparoscopic cholecystectomy
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bites and stings
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bite force
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female infertility
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dyslipidemias
Bevifimod
hemophilia a
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Pegtibatinase
homocystinuria
Globulin, immune
large b-cell lymphoma diffuse
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b-cell lymphoma
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lymphoma
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leukemia
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lymphoid leukemia
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multiple myeloma
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plasma cell neoplasms
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precursor cell lymphoblastic leukemia-lymphoma
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multiple sclerosis
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sclerosis
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b-cell chronic lymphocytic leukemia
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prolymphocytic leukemia
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kidney diseases
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membranous glomerulonephritis
Talfirastide
hypertension
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graft rejection
Bradykinin
hereditary angioedemas
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angioedema
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